transfusion-dependent beta thalassemia - SERP Analysis

https://www.bluebirdbio.com/our-focus/beta-thalassemia

https://medlineplus.gov/genetics/condition/beta-thalassemia/

https://pmc.ncbi.nlm.nih.gov/articles/PMC6142569/

https://www.chop.edu/treatments/gene-therapy-transfusion-dependent-beta-thalassemia

https://www.lifewithbetathal.com/transfusion-dependence/impact-and-symptoms

https://www.sciencedirect.com/science/article/pii/S0268960X23000991

https://www.challengetdt.com/

https://www.nejm.org/doi/full/10.1056/NEJMoa2309673

https://pmc.ncbi.nlm.nih.gov/articles/PMC9345633/

https://www.childrenshospital.org/conditions/thalassemia

https://ashpublications.org/blood/article/143/10/930/498767/Pretransfusion-hemoglobin-level-and-mortality-in

https://onlinelibrary.wiley.com/doi/full/10.1002/ajh.27166

https://www.casgevy.com/beta-thalassemia

https://en.wikipedia.org/wiki/Beta_thalassemia

https://www.frontiersin.org/journals/hematology/articles/10.3389/frhem.2023.1187681/full

https://www.cdc.gov/thalassemia/communication-resources/initiating-regular-transfusions.html

https://ashpublications.org/blood/article/142/11/949/497012/How-I-treat-non-transfusion-dependent-thalassemia

https://www.nejm.org/doi/full/10.1056/NEJMoa1705342

https://www.rethinkthalassemia.com/complications/transfusion-dependent-thalassemia

https://thalassaemia.org.cy/publications/tif-publications/guidelines-for-the-management-of-transfusion-dependent-%CE%B2-thalassaemia-5th-edition-2025/

https://www.aabb.org/docs/default-source/default-document-library/resources/association-bulletins/ab23-02.pdf?sfvrsn=1f310ce5_6

https://www.vjhemonc.com/video/jjfmyj3nfse-treating-transfusion-dependent-and-independent-beta-thalassemia-and-believebeyond-trial-updates/

https://www.sciencedirect.com/science/article/pii/S0006497119826113

https://www.icliniq.com/articles/blood-health/transfusion-dependent-beta-thalassemia

https://www.sharecare.com/genetic-disorders-birth-defects/treatment-transfusion-dependent-thalassemia

https://www.youtube.com/watch?v=JJfmYj3NFsE

https://www.ajmc.com/view/exagamglogene-autotemcel-shows-promise-in-treatment-of-transfusion-dependent--thalassemia

https://taylorandfrancis.com/knowledge/Medicine_and_healthcare/Hematology/Transfusion-dependent_anemia/

https://www.thelancet.com/journals/lancet/article/PIIS0140-6736(24)01884-1/fulltext

https://www.nature.com/articles/s41392-025-02135-9

https://www.moh.gov.my/moh/attachments/3926.pdf

https://onlinelibrary.wiley.com/doi/10.1111/trf.16640

https://thalassaemia.org.cy/wp-content/uploads/2022/08/TDT-GUIDE-2022-FOR-web.pdf

https://www.uptodate.com/contents/management-of-thalassemia

https://www.healthcentral.com/slideshow/two-new-cures-for-transfusion-dependent-beta-thalassemia

https://www.gov.uk/government/news/mhra-authorises-world-first-gene-therapy-that-aims-to-cure-sickle-cell-disease-and-transfusion-dependent-thalassemia

https://www.ajmc.com/view/high-health-care-burden-of-transfusion-dependent--thalassemia

https://presse.inserm.fr/en/sickle-cell-disease-and-transfusion-dependent-beta-thalassemia-promising-results-of-gene-therapy-treatment/60473/

https://www.stgeorges.nhs.uk/wp-content/uploads/2020/02/TIF-guidelines-for-the-management-of-Transfusion-Dependent-Thalassaemia-2014.pdf

https://www.youtube.com/watch?v=C_IypMNe5JA

https://www.cdc.gov/thalassemia/hcp/toolkit/developing-a-transfusion-plan.html

https://www.nice.org.uk/guidance/indevelopment/gid-ta10334

https://www.europeanpharmaceuticalreview.com/news/168815/%CE%B2-thalassemia-patients-achieve-transfusion-independence-with-gene-therapy/

https://www.vjhemonc.com/video/bcamlenywek-a-global-view-of-transfusion-dependent-thalassemia-standard-of-care-outcomes-and-unmet-needs/

https://www.moh.gov.my/moh/attachments/8318.pdf

https://europepmc.org/article/pmc/pmc8523624

https://www.mayoclinic.org/diseases-conditions/thalassemia/symptoms-causes/syc-20354995

https://www.youtube.com/watch?v=lwOaOo1ckKc

https://my.clevelandclinic.org/health/diseases/14508-thalassemias

https://www.nice.org.uk/guidance/discontinued/gid-ta10334

https://synapse.patsnap.com/disease/42e70d35b3054821a8a726271abda051

https://www.healthcentral.com/slideshow/transfusion-dependent-beta-thalassemia-treatment

https://www.hopkinsmedicine.org/health/conditions-and-diseases/beta-thalassemia

https://www.nature.com/articles/jhg2013131

https://www.ispor.org/docs/default-source/intl2023/ispor23boateng-kuffourpcr132125262-pdf.pdf?sfvrsn=60a84254_0

https://en.wikipedia.org/wiki/Transfusion-dependent_anemia

https://www.newsgd.com/node_99363c4f3b/2689900651.shtml

https://www.youtube.com/watch?v=gJeA_RKTeeE

https://www.cgtlive.com/view/around-the-helix-cell-and-gene-therapy-company-updates-june-18-2025

https://www.thieme-connect.com/products/ejournals/pdf/10.1055/s-0040-1703903.pdf

https://www.tsh.or.th/file_upload/files/09(4).pdf

https://www.youtube.com/watch?v=dQ9afCfzBQE

https://www.cgtlive.com/view/top-news-expert-insights-world-sickle-cell-day-2025

https://www.youtube.com/watch?v=hz2Yoiwi8Pw

https://clinicaltrials.gov/study/NCT05757700

https://crisprtx.com/

https://www.youtube.com/watch?v=6emOCXysZZc

https://www.pharmiweb.com/press-release/2025-06-21/gene-therapies-for-hematologic-disorders-market-to-reach-285-billion-by-2025-fueled-by-accelerating-innovation-and-regulatory-tailwinds

https://www.rttnews.com/3547037/agios-pyrukynd-faces-fda-review-in-september-expansion-opportunity-ahead.aspx

https://www.ablesci.com/assist/detail?id=4EeXnY

https://www.biospace.com/press-releases/vertex-and-ono-pharmaceutical-announce-strategic-agreement-to-develop-and-commercialize-povetacicept-in-japan-and-south-korea

https://www.webmd.com/a-to-z-guides/beta-thalassemia-blood-transfusions

https://pipelinereview.com/ono-pharmaceutical-and-vertex-announce-strategic-agreement-to-develop-and-commercialize-povetacicept-in-japan-and-south-korea/

https://www.youtube.com/watch?v=uzZoAoz4pIw

https://www.biospace.com/press-releases/ono-pharmaceutical-and-vertex-announce-strategic-agreement-to-develop-and-commercialize-povetacicept-in-japan-and-south-korea

https://finance.yahoo.com/quote/CRSP/

https://www.youtube.com/watch?v=_ACJvHTtQJ4

https://newshub.medianet.com.au/2025/06/vertex-announces-expanded-reimbursement-agreement-in-australia-for-trikafta-elexacaftor-tezacaftor-ivacaftor-and-ivacaftor-for-people-with-cystic-fibrosis/106662/

https://www.morningstar.com/news/business-wire/20250623305587/ono-pharmaceutical-and-vertex-announce-strategic-agreement-to-develop-and-commercialize-povetacicept-in-japan-and-south-korea

https://news.vrtx.com/news-releases/news-release-details/vertex-presents-positive-data-zimislecel-type-1-diabetes

https://www.stocktitan.net/news/VRTX/vertex-and-ono-pharmaceutical-announce-strategic-agreement-to-ct75hnc9j8wh.html

https://www.directorstalkinterviews.com/crispr-therapeutics-ag-crsp-stock-analysis-a-biotech-leader-with-71-6-revenue-growth-and-promising-gene-editing-innovations/4121203981

https://www.theglobeandmail.com/investing/markets/stocks/VRTX/pressreleases/32892609/3-growth-stocks-you-can-buy-right-now-without-any-hesitation/

https://www.youtube.com/watch?v=rNWEj70Tdno

https://www.mdpi.com/2077-0383/14/13/4476

https://markets.ft.com/data/announce/detail?dockey=600-202506230400BIZWIRE_USPRX____20250623_BW239210-1

https://finance.yahoo.com/quote/AGIO/

https://diabetesjournals.org/care/article/48/Supplement_1/S27/157566/2-Diagnosis-and-Classification-of-Diabetes

https://www.youtube.com/watch?v=9gKjFAGTc00

https://www.facebook.com/tif.thalassaemia/videos/the-5th-edition-of-the-tif-guidelines-for-the-management-of-transfusion-dependen/992279029337897/

https://library.ehaweb.org/eha/2019/24th/266726/emilia.ursu.dental.health.status.in.patients.with.hemophilia.single.center.html

https://kidshealth.org/en/parents/beta-thalassemia.html

https://www.mdpi.com/2227-9032/13/13/1500

https://www.cnn.gr/oikonomia/nea-tis-agoras/story/482764/v-thalassaimia-i-spania-nosos-me-sovares-synepeies-gia-tous-astheneis-tis-oikogeneies-tin-koinonia

https://www.gurufocus.com/news/2938082/vertex-presents-positive-data-for-zimislecel-in-type-1-diabetes-at-the-american-diabetes-association-85th-scientific-sessions

https://labtestsonline.org.uk/tests/full-blood-count-fbc

https://markets.ft.com/data/announce/detail?dockey=600-202506201915BIZWIRE_USPRX____20250620_BW485709-1

https://www.youtube.com/watch?v=lle5xzI32cM

https://www.newswiretoday.com/news/184195/Ono-Pharmaceutical-and-Vertex-Announce-Strategic-Agreement-to-Develop-and-Commercialize-Povetacicept-in-Japan-and-South-Korea/